Genes and Pathways Regulated by Androgens in Human Neural Cells, Potential Candidates for the Male Excess in Autism Spectrum Disorder
Generation of a human induced pluripotent stem cell line (iPSC) from peripheral blood mononuclear cells of a patient with a myasthenic syndrome due to mutation in COLQ
AAV2/9-mediated silencing of PMP22 prevents the development of pathological features in a rat model of Charcot-Marie-Tooth disease 1 A
Myogenesis modelled by human pluripotent stem cells: a multi-omic study of Duchenne myopathy early onset
Exosomes: Multi-faceted natural intercellular messengers as new candidates for the treatment of myopathies?