Dr. Françoise Piguet : Gene therapy of lysosomal storage disorders and new AAV vectors and tools to optimize BBB targeting.
The DrugCell lance son programme de recherche et d’industrialisation dans le domaine des thérapies cellulaires
Pr. Stephanie Cherqui : From Cystinosis to Alzheimer’s Disease: Lessons Learned Treating a Rare Metabolic Disease Using Hematopoietic Stem Cell Gene Therapy.
